137-0
INTERNATIONAL CROSS-SECTIONAL STUDY ON OUTCOME AND THERAPEUTIC EFFICACY IN GLUTARIC ACIDURIA TYPE I (GA-I)
Kolker S, Greenberg CR, Leonard JV, Saudubray JM, Kalkanoglu HS, Walter JH, Lagler F, Schwahn B, Troncoso M, Chalmers RA, Lund A, Koeller D, Burlina A, Wajner M, Christensen E, Zschocke...
08 octubre, 2022
/